NHS to offer 'world's most expensive' £1.8m-a-dose drug to cure baby spinal disease

NHS to offer 'world's most expensive' £1.8m-a-dose drug to cure baby spinal disease Babies born with a genetic disease that can lead to a life expectancy of just two years without intervention will now be cured on the NHS with a new £1.8million drug.

Around 56 infants are born with severe spinal muscular atrophy (SMA) in England every year, which causes muscle weakness and can lead to paralysis.

The National Institute for Health and Care Excellence (Nice), the NHS watchdog, has approved the use of onasemnogene abeparvovec, branded as Zolgensma, for babies born with the condition. The Daily Mail