Gene therapy cures babies of rare ‘bubble boy’ immune disorder in world first

Gene therapy cures babies of rare ‘bubble boy’ immune disorder in world first Ten newborns with the rare genetic disorder known as “bubble boy” disease were cured with gene therapy, researchers said on Wednesday.

The treatment appears to have completely rid the babies of their immune disorder with no side effects or complications – a result scientists have sought for decades through painstaking research and heartbreaking setbacks. The Independent

See also:

• St. Jude gene therapy cures babies with 'bubble boy' disease St Jude Children's Research Hospital
• HIV used to cure 'bubble boy' disease BBC News