First toddler receives life-saving gene therapy on NHS

First toddler receives life-saving gene therapy on NHS Teddi from Northumberland with a rare and devastating genetic condition has become the first child to be treated on the NHS with a life-saving gene therapy.

The drug, called Libmeldy, is the most expensive medicine ever approved for the NHS. BBC News

See also:

• NHS to roll out life-saving gene therapy for rare disease affecting babies NHS England
• The UK’s most expensive drug saved one sister, but it is too late for the other BBC News
• Little Teddi becomes the first child to receive revolutionary gene therapy drug on the NHS The Daily Mail
• Girl with deadly inherited condition is cured with gene therapy on NHS The Guardian
• Heartbreak as one sibling saved using miracle drug, but older sister not eligible for treatment The Independent